Search for Clinical Trial Results
Deficiency Diseases - 55 Studies Found
Status | Study |
Completed |
Study Name: IMM 0212: Busulfan With Fludarabine and Antithymocyte Globulin as Preparative Therapy for Hematopoietic Stem Cell Transplant for the Treatment of Severe Congenital T-Cell Immunodeficiency Condition:
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Completed |
Study Name: Construction of a Health-related Quality of Life (HR-QOL) Questionnaire for Patients With Primary Antibody Deficiency Disease Condition: Immune Deficiency, Antibody Date: 2015-08-31 Interventions: Other: questionnaire survey The HR-QOL PIDD survey will be administered to the patient by the site PI or |
Completed |
Study Name: GTA-Glyceryltriacetate for Canavan Disease Condition:
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Recruiting |
Study Name: International Collaborative Gaucher Group (ICGG) Gaucher Registry Condition:
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Completed |
Study Name: A Multicenter Study of the Efficacy of Cerezyme in Testing Skeletal Disease in Patients With Type I Gaucher Disease. Condition:
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Completed |
Study Name: Safety and Efficacy of Cerezyme® Infusions Every 4 Weeks Versus Every 2 Weeks in Type 1 Gaucher Disease Condition:
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Completed |
Study Name: A Study of the Efficacy and Safety of Eliglustat Tartrate (Genz-112638) in Type 1 Gaucher Patients Condition:
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Active, not recruiting |
Study Name: Growth and Development Study of Alglucosidase Alfa. Condition:
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Withdrawn |
Study Name: Lithium and Acetate for Canavan Disease Condition:
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Approved for marketing |
Study Name: Alglucosidase Alfa Temporary Access Program Condition:
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